Hemgenix, a single-dose cure for a form of the blood-clotting disorder hemophilia, recently set a new world record for the most expensive drug ever at a whopping $3.5 million per dose.
On Tuesday, The US Food and Drug Administration approved Hemgenix, a cutting-edge gene therapy designed to treat adults with hemophilia B, a serious genetic disorder in which people do not produce a critical protein needed to clot blood in case of bleeding. Until now, typical treatments required routine injections to maintain sufficient levels of the missing protein in patients, but thanks to Hemgenix, sufferers of hemophilia B require a single IV infusion to be cured forever. The only problem is that that single dose costs no less than $3.5 million, making Hemgenix the most expensive drug ever.
